BioCentury | Aug 15, 2019
Distillery Therapeutics
TMED9 inhibition for mucin 1 kidney disease
...stem (iPS) cells. The TMED9 inhibitor also produced misfolded protein removal from cells expressing mutant UMOD...
...the kidneys. TARGET/MARKER/PATHWAY: Mucin 1 (MUC1; CD227); transmembrane p24 trafficking protein 9 (TMED9); uromodulin (UMOD; THP...
...School, Boston, Mass. email: agreka@broadinstitute.org Claire Quang Broad Institute of MIT and Harvard Mucin 1 (MUC1) (CD227) Rhodopsin (RHO) (OPN2) Uromodulin (UMOD) (THP) Retinitis Renal...
...the kidneys. TARGET/MARKER/PATHWAY: Mucin 1 (MUC1; CD227); transmembrane p24 trafficking protein 9 (TMED9); uromodulin (UMOD; THP...
...School, Boston, Mass. email: agreka@broadinstitute.org Claire Quang Broad Institute of MIT and Harvard Mucin 1 (MUC1) (CD227) Rhodopsin (RHO) (OPN2) Uromodulin (UMOD) (THP) Retinitis Renal...