BioCentury | Sep 4, 2019
Company News

Novartis’ early collaboration with NICE key to rapid response on Luxturna

...develop and commercialize Luxturna outside the U.S. Luxturna is an adeno-associated virus (AAV) delivering the retinal pigment epithelium-specific protein 65kDa (RPE65)...
BioCentury | Jun 17, 2019
Company News

Trial data suggest 80% of Zynteglo patients could meet milestones in outcomes-based pricing model

...SIX:ROG; OTCQX:RHHBY), priced Luxturna voretigene neparvovec-rzyl at $425,000 per eye to treat patients with biallelic retinal pigment epithelium-specific protein 65kDa (RPE65)...
BioCentury | Apr 26, 2019
Product Development

Rise of the independents, biotechs go to market

...an in vivo gene therapy with Luxturna voretigene neparvovec-rzyl in December 2017 to treat biallelic retinal pigment epithelium-specific protein 65kDa (RPE65)...
BioCentury | Mar 1, 2019
Company News

Spark gives Roche beachhead in gene therapy

...lead program is Luxturna voretigene neparvovec-rzyl, which FDA approved in December 2017 to treat biallelic retinal pigment epithelium-specific protein 65kDa (RPE65)...
BioCentury | Feb 25, 2019
Company News

Spark gives Roche beachhead in gene therapy

...lead program is Luxturna voretigene neparvovec-rzyl, which FDA approved in December 2017 to treat biallelic retinal pigment epithelium-specific protein 65kDa (RPE65)...
BioCentury | Feb 13, 2019
Company News

Spark elaborates on proposed Luxturna value-based pricing model

...Intermediate Value, Discusses Pricing Models" ). FDA approved Luxturna in December 2017 to treat biallelic retinal pigment epithelium-specific protein 65kDa (RPE65)...
BioCentury | Feb 1, 2019
Politics, Policy & Law

Focusing on cures

...that treats patients with vision loss due to genetic mutations in both copies of the retinal pigment epithelium-specific protein 65kDa (RPE65)...
BioCentury | Nov 30, 2018
Clinical News

Luxturna gets EU approval

...to treat patients with vision loss due to genetic mutation in both copies of the retinal pigment epithelium-specific protein 65kDa (RPE65)...
...Philadelphia, Pa. Product: Luxturna voretigene neparvovec Business: Ophthalmic Chris Lieu AAV2-hRPE65v2, Luxturna, voretigene neparvovec-rzyl (spk-rpe65) Novartis AG Spark Therapeutics Inc. Retinal pigment epithelium-specific protein 65kDa (RPE65) Blindness...
BioCentury | Sep 28, 2018
Clinical News

CHMP backs Luxturna, Lilly's migraine mAb, antibiotic Vabomere

...Luxturna received CHMP's recommendation to treat adults and children with inherited retinal dystrophy caused by retinal pigment epithelium-specific protein 65kDa (RPE65)...
...c-Met proto-oncogene) Calcitonin gene-related peptide (CGRP) CC chemokine receptor 4 (CCR4) (CD194) Dystrophin Epidermal growth factor receptor (EGFR) (ErbB1) (HER1) Retinal pigment epithelium-specific protein 65kDa (RPE65) Sphingosine...
BioCentury | Sep 21, 2018
Company News

CHMP backs Luxturna, Lilly's migraine mAb, antibiotic Vabomere

...Luxturna received CHMP's recommendation to treat adults and children with inherited retinal dystrophy caused by retinal pigment epithelium-specific protein 65kDa (RPE65)...
...c-Met proto-oncogene) Calcitonin gene-related peptide (CGRP) CC chemokine receptor 4 (CCR4) (CD194) Dystrophin Epidermal growth factor receptor (EGFR) (ErbB1) (HER1) Retinal pigment epithelium-specific protein 65kDa (RPE65) Sphingosine...
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