13:23 , May 31, 2017 |  BC Innovations  |  Distillery Therapeutics

Musculoskeletal

INDICATION: Muscular dystrophy Patient sample, zebrafish and dog studies suggest inhibiting PITPNA could help treat Duchenne muscular dystrophy (DMD). In primary myoblasts derived from DMD patients, PITPNA knockdown increased fusion index in muscle fibers, a...