BC Innovations | Jan 23, 2019
Distillery Therapeutics

Cardiovascular

INDICATION: Cardiomyopathy Patient sample studies suggest CRISPR-mediated editing of the B isoform of LAMP2 could help treat Danon disease, a cardiomyopathy caused by a loss-of-function LAMP2 point mutations. In cardiomyocytes from patients, CRISPR-Cas9-mediated correction of...
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