02:37 , Sep 14, 2018 |  BC Innovations  |  Product R&D

Academia’s manufacturing problem

With backups at academic manufacturing centers beginning to hamper translation of early stage gene therapies, pushing those who can afford it to CMOs, at least one non-profit has stepped in with a model to deliver...
17:38 , Jul 17, 2018 |  BC Innovations  |  Distillery Therapeutics

Otologic

INDICATION: Hearing loss Mouse studies suggest CLRN1 gene therapy could help treat hearing loss in Usher syndrome type 3A, which is caused by CLRN1 mutations. In a hair cell-specific CLRN1 knockout mouse model of Usher...
07:00 , Apr 28, 2016 |  BC Innovations  |  Distillery Therapeutics

Therapeutics: Clarin 1 (CLRN1)

Other INDICATION: Hearing loss In vitro and mouse studies identified a CLRN1 protein stabilizer that could help treat hearing loss in patients with Usher syndrome type III. High throughput screening of a small molecule library...