BC Innovations | Sep 14, 2018
Product R&D

Academia’s manufacturing problem

With backups at academic manufacturing centers beginning to hamper translation of early stage gene therapies, pushing those who can afford it to CMOs, at least one non-profit has stepped in with a model to deliver...
BC Innovations | Jul 17, 2018
Distillery Therapeutics


INDICATION: Hearing loss Mouse studies suggest CLRN1 gene therapy could help treat hearing loss in Usher syndrome type 3A, which is caused by CLRN1 mutations. In a hair cell-specific CLRN1 knockout mouse model of Usher...
BC Innovations | Apr 28, 2016
Distillery Therapeutics

Therapeutics: Clarin 1 (CLRN1)

Other INDICATION: Hearing loss In vitro and mouse studies identified a CLRN1 protein stabilizer that could help treat hearing loss in patients with Usher syndrome type III. High throughput screening of a small molecule library...
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