23:17 , Oct 3, 2018 |  BC Innovations  |  Translation in Brief

New Therapeutic Targets and Biomarkers: September 2018

New Therapeutic Targets and Biomarkers: September 2018 Select top therapeutic targets and biomarkers covered by BioCentury or added to the BCIQ database in September. Therapeutic targets are defined as any protein, gene or other molecule...
19:32 , Sep 10, 2018 |  BC Innovations  |  Distillery Therapeutics

Endocrine/metabolic

INDICATION: Metabolic Mouse studies suggest ASL gene therapy could help treat argininosuccinic aciduria, which is caused by ASL mutations. In a mouse model of the disease, an adeno-associated viral (AAV) serotype 8 (AAV8) vector encoding...