07:00 , Apr 28, 2014 |  BC Week In Review  |  Clinical News

AAV8 vector encoding GUCY2D gene regulatory update

The European Commission granted Orphan Drug designation for Fondazione Telethon's adeno-associated virus (AAV) serotype 8 vector encoding the human guanylate cyclase 2D membrane retina-specific (GUCY2D) gene to treat Leber's congenital amaurosis (LCA). The company could...