BioCentury | Dec 22, 2020
Politics, Policy & Law

Budget bill extends pediatric priority review vouchers, boosts NIH, FDA

...to be approved even if they were not clinically superior to approved orphan drugs. The National Organization for Rare Disorders...
BioCentury | Jul 24, 2020
Regulation

PDUFA VII to be shaped by COVID-19 experience

...on where resources are allocated. Rachel Sher, VP of regulatory and government affairs at the National Organization for Rare Disorders...
BioCentury | Apr 4, 2020
Product Development

Patient groups call out silver linings that could emerge from COVID-19 crisis

...the ability to deduct charitable donations. Lauren Martz, Senior Editor Multiple Myeloma Research Foundation (MMRF) National Multiple Sclerosis Society National Organization for Rare Disorders COVID-19 cov19count cov19pol cov19count cov19pol...
BioCentury | Feb 8, 2020
Politics, Policy & Law

GAO finds little evidence Priority Review program spurring drug development

...Gates Foundation, BIO, Drugs for Neglected Diseases Initiative, Médecins Sans Frontières, Medicines for Malaria Ventures, National Organization for Rare Disorders...
BioCentury | Jan 29, 2020
Politics & Policy

House bill seeks to tweak Orphan Drug Act, could pose threat to pathway

...of medicines for rare diseases.” Rachel Sher, VP for policy and regulatory affairs at the National Organization for Rare Disorders...
BioCentury | Dec 2, 2019
Politics & Policy

Patient, medical groups urge quick confirmation of Hahn as FDA commissioner

...ACS CAN); American Society of Clinical Oncology (ASCO); Friends of Cancer Research; Melanoma Research Foundation; National Organization for Rare Disorders...
BioCentury | Nov 13, 2019
Finance

Allievex, backed by Pappas and Novo, scoops up BioMarin ultra-rare disease assets

...Mathers, Pappas and Allievex MPS IIIB affects about one in 200,000 births, according to the National Organization for Rare Disorders...
BioCentury | Oct 24, 2019
Finance

Allievex, backed by Pappas and Novo, scoops up BioMarin ultra-rare disease assets

...Mathers, Pappas and Allievex MPS IIIB affects about one in 200,000 births, according to the National Organization for Rare Disorders...
BioCentury | Jun 26, 2019
Politics & Policy

Senate committee passes bill squeezing PBMs, attacking anticompetitive drug company practices

...be approved even if they were not clinically superior to an approved orphan drug. The National Organization for Rare Disorders...
BioCentury | Jun 26, 2019
Politics & Policy

HELP Committee advances transparency bill

...benefit managers (PBM's), health insurers and hospitals.” Steve Usdin, Washington Editor Pharmaceutical Research and Manufacturers of America (PhRMA) National Organization for Rare Disorders Biotechnology...
Items per page:
1 - 10 of 97
BioCentury | Dec 22, 2020
Politics, Policy & Law

Budget bill extends pediatric priority review vouchers, boosts NIH, FDA

...to be approved even if they were not clinically superior to approved orphan drugs. The National Organization for Rare Disorders...
BioCentury | Jul 24, 2020
Regulation

PDUFA VII to be shaped by COVID-19 experience

...on where resources are allocated. Rachel Sher, VP of regulatory and government affairs at the National Organization for Rare Disorders...
BioCentury | Apr 4, 2020
Product Development

Patient groups call out silver linings that could emerge from COVID-19 crisis

...the ability to deduct charitable donations. Lauren Martz, Senior Editor Multiple Myeloma Research Foundation (MMRF) National Multiple Sclerosis Society National Organization for Rare Disorders COVID-19 cov19count cov19pol cov19count cov19pol...
BioCentury | Feb 8, 2020
Politics, Policy & Law

GAO finds little evidence Priority Review program spurring drug development

...Gates Foundation, BIO, Drugs for Neglected Diseases Initiative, Médecins Sans Frontières, Medicines for Malaria Ventures, National Organization for Rare Disorders...
BioCentury | Jan 29, 2020
Politics & Policy

House bill seeks to tweak Orphan Drug Act, could pose threat to pathway

...of medicines for rare diseases.” Rachel Sher, VP for policy and regulatory affairs at the National Organization for Rare Disorders...
BioCentury | Dec 2, 2019
Politics & Policy

Patient, medical groups urge quick confirmation of Hahn as FDA commissioner

...ACS CAN); American Society of Clinical Oncology (ASCO); Friends of Cancer Research; Melanoma Research Foundation; National Organization for Rare Disorders...
BioCentury | Nov 13, 2019
Finance

Allievex, backed by Pappas and Novo, scoops up BioMarin ultra-rare disease assets

...Mathers, Pappas and Allievex MPS IIIB affects about one in 200,000 births, according to the National Organization for Rare Disorders...
BioCentury | Oct 24, 2019
Finance

Allievex, backed by Pappas and Novo, scoops up BioMarin ultra-rare disease assets

...Mathers, Pappas and Allievex MPS IIIB affects about one in 200,000 births, according to the National Organization for Rare Disorders...
BioCentury | Jun 26, 2019
Politics & Policy

Senate committee passes bill squeezing PBMs, attacking anticompetitive drug company practices

...be approved even if they were not clinically superior to an approved orphan drug. The National Organization for Rare Disorders...
BioCentury | Jun 26, 2019
Politics & Policy

HELP Committee advances transparency bill

...benefit managers (PBM's), health insurers and hospitals.” Steve Usdin, Washington Editor Pharmaceutical Research and Manufacturers of America (PhRMA) National Organization for Rare Disorders Biotechnology...
Items per page:
1 - 10 of 97