BioCentury | Oct 23, 2020
Finance

Sarepta joins investor trio in Aavanti’s $107M series A round to develop gene therapy for Friedreich’s ataxia

...the series A round, AavantiBio received backing from Italian patient advocacy group GoFAR and the Muscular Dystrophy Association...
BioCentury | Mar 24, 2020
Product Development

Positive data for intrathecally delivered Zolgensma could broaden its patient population

...new entrant in the coming months. During a virtual Clinical Trial Session conducted by the Muscular Dystrophy Association...
BioCentury | Dec 11, 2019
Company News

Management tracks: Elevate hires CSO of regenerative medicine; plus BridgeBio, Acceleron, Flexion, Locana, Nkarta and more

...previously served as director of NIH's National Center for Complementary and Integrative Health. The non-profit Muscular Dystrophy Association...
...Li and Elizabeth S. Eaton, Staff Writers BridgeBio Pharma Inc. Acceleron Pharma Inc. Replimune Group Inc. Stemline Therapeutics Inc. Nkarta Inc. Muscular Dystrophy Association Locana...
BioCentury | Sep 27, 2019
Company News

Management tracks: Neurogene, HomoShear, Hookipa, Passage Bio, Artios, EMD Serono, Novartis, Illumina, Precision and CureDuchenne

...Lianna Orlando as senior director of research. She was interim head of research at the Muscular Dystrophy Association. BioCentury...
BioCentury | Sep 27, 2019
Product Development

Lessons from Healey ALS on how to build platform trials quickly

...a platform trial. Qhreshi pointed to muscular dystrophy as an example. In July 2018, the Muscular Dystrophy Association...
BioCentury | Apr 17, 2019
Clinical News

Ionis slides after AveXis reports SMA data for Zolgensma

...ENDEAR achieved a 4-point improvement in CHOP-INTEND score. The STR1VE data were presented at the Muscular Dystrophy Association...
BioCentury | Apr 16, 2019
Clinical News

Wave down on Phase I safety data for DMD therapy

...suvodirsen in 2020. Wave presented the Phase I data and Phase II/III design at the Muscular Dystrophy Association...
BioCentury | Mar 8, 2019
Clinical News

Santhera's Raxone slows loss of respiratory function in real-world DMD study

...to EMA for Raxone to treat DMD. Data from SYROS will be presented at the Muscular Dystrophy Association...
...Staff Writer Sovrima (Brand), Raxone (Brand), Catena (Brand), SNT-MC17 (Compound #), idebenone (Generic), Raxone (Other), Catena (Other) Muscular Dystrophy Association Santhera...
BioCentury | Jun 21, 2018
Company News

Sarepta says no to right to try for its DMD therapies

...approved, and compassionate use won't be necessary," Miller said. Parent Project Muscular Dystrophy and the Muscular Dystrophy Association...
BioCentury | Apr 20, 2018
Company News

Target ALS and partners launch biomarker study

...Target ALS Foundation (New York, N.Y.) is partnering with the Muscular Dystrophy Association (MDA) (Chicago, Ill.), the CReATe...
...N.Y. Muscular Dystrophy Association, Chicago, Ill. Business: Neurology Mary Romeo Amgen Inc. Biogen Inc. Denali Therapeutics Inc. Genentech Inc. Genzyme Corp. Merck & Co. Inc. Muscular Dystrophy Association Roche Sanofi Takeda...
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BioCentury | Oct 23, 2020
Finance

Sarepta joins investor trio in Aavanti’s $107M series A round to develop gene therapy for Friedreich’s ataxia

...the series A round, AavantiBio received backing from Italian patient advocacy group GoFAR and the Muscular Dystrophy Association...
BioCentury | Mar 24, 2020
Product Development

Positive data for intrathecally delivered Zolgensma could broaden its patient population

...new entrant in the coming months. During a virtual Clinical Trial Session conducted by the Muscular Dystrophy Association...
BioCentury | Dec 11, 2019
Company News

Management tracks: Elevate hires CSO of regenerative medicine; plus BridgeBio, Acceleron, Flexion, Locana, Nkarta and more

...previously served as director of NIH's National Center for Complementary and Integrative Health. The non-profit Muscular Dystrophy Association...
...Li and Elizabeth S. Eaton, Staff Writers BridgeBio Pharma Inc. Acceleron Pharma Inc. Replimune Group Inc. Stemline Therapeutics Inc. Nkarta Inc. Muscular Dystrophy Association Locana...
BioCentury | Sep 27, 2019
Company News

Management tracks: Neurogene, HomoShear, Hookipa, Passage Bio, Artios, EMD Serono, Novartis, Illumina, Precision and CureDuchenne

...Lianna Orlando as senior director of research. She was interim head of research at the Muscular Dystrophy Association. BioCentury...
BioCentury | Sep 27, 2019
Product Development

Lessons from Healey ALS on how to build platform trials quickly

...a platform trial. Qhreshi pointed to muscular dystrophy as an example. In July 2018, the Muscular Dystrophy Association...
BioCentury | Apr 17, 2019
Clinical News

Ionis slides after AveXis reports SMA data for Zolgensma

...ENDEAR achieved a 4-point improvement in CHOP-INTEND score. The STR1VE data were presented at the Muscular Dystrophy Association...
BioCentury | Apr 16, 2019
Clinical News

Wave down on Phase I safety data for DMD therapy

...suvodirsen in 2020. Wave presented the Phase I data and Phase II/III design at the Muscular Dystrophy Association...
BioCentury | Mar 8, 2019
Clinical News

Santhera's Raxone slows loss of respiratory function in real-world DMD study

...to EMA for Raxone to treat DMD. Data from SYROS will be presented at the Muscular Dystrophy Association...
...Staff Writer Sovrima (Brand), Raxone (Brand), Catena (Brand), SNT-MC17 (Compound #), idebenone (Generic), Raxone (Other), Catena (Other) Muscular Dystrophy Association Santhera...
BioCentury | Jun 21, 2018
Company News

Sarepta says no to right to try for its DMD therapies

...approved, and compassionate use won't be necessary," Miller said. Parent Project Muscular Dystrophy and the Muscular Dystrophy Association...
BioCentury | Apr 20, 2018
Company News

Target ALS and partners launch biomarker study

...Target ALS Foundation (New York, N.Y.) is partnering with the Muscular Dystrophy Association (MDA) (Chicago, Ill.), the CReATe...
...N.Y. Muscular Dystrophy Association, Chicago, Ill. Business: Neurology Mary Romeo Amgen Inc. Biogen Inc. Denali Therapeutics Inc. Genentech Inc. Genzyme Corp. Merck & Co. Inc. Muscular Dystrophy Association Roche Sanofi Takeda...
Items per page:
1 - 10 of 34